Aceneuramic acid is the first approved drug for GNE myopathy treatment

A clinical trial has led to the approval of a treatment for patients with a rare, muscle-weakening disease called GNE myopathy.

A clinical trial has led to the approval of a treatment for patients with a rare, muscle-weakening disease called GNE myopathy.

Read more https://www.sciencedaily.com/releases/2024/08/240820124529.htm